Frequency and phenotypic characteristics of RPE65 mutations in the Chinese population | Orphanet Journal of Rare Diseases | Full Text
Luxturna: A Gene Therapy Reviving Retinal Cells in Children with Leber Congenital Amaurosis | Arizona RETINA Project
RPE65 - an overview | ScienceDirect Topics
Gene therapy: 'Now I can see my own face again' - BBC News
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial - The Lancet
Overview of RPE65 mutations reported to date in the Chinese population... | Download Scientific Diagram
IJMS | Free Full-Text | An Update on Gene Therapy for Inherited Retinal Dystrophy: Experience in Leber Congenital Amaurosis Clinical Trials
Gene therapy for RPE65-mediated inherited retinal dystrophy completes phase 3 - The Lancet
RPE65 gene - Gene Vision
A New Gene Therapy For Early-onset RP
AZ RETINA Project on X: "This happens by restoring the missing enzyme in RPE. The treatment is injected past the neural retina, so it interacts with the RPE. Recently, there has been
RPE65 - retinal degeneration: for patients - Gene Vision
Persistence of non-viral vector mediated RPE65 expression: Case for viability as a gene transfer therapy for RPE-based diseases - ScienceDirect
RPE65 Gene - GeneCards | RPE65 Protein | RPE65 Antibody
Benefits of gene therapy for both eyes - The Lancet
A New Gene Therapy For Early-onset RP
Gene therapy in Rpe65 / mice at advanced disease stages leads to... | Download Scientific Diagram
RPE65-related retinal dystrophy: mutational and phenotypic spectrum in 45 affected patients | medRxiv
Gene Therapy for Inherited Retinal Disease
NIH scientists discover essential step in recharging the eye's light-sensing retina | National Institutes of Health (NIH)
Retinal pigment epithelium 65 kDa protein (RPE65): An update - ScienceDirect
RPE65 - an overview | ScienceDirect Topics
A Novel Mutation in the RPE65 Gene Causing Leber Congenital Amaurosis and Its Transcriptional Expression In Vitro | PLOS ONE
RPE65 - Wikipedia
RPE65 Gene - GeneCards | RPE65 Protein | RPE65 Antibody
Cells | Free Full-Text | The Predicted Splicing Variant c.11+5G>A in RPE65 Leads to a Reduction in mRNA Expression in a Cell-Specific Manner
